Fixing stem cells via genome editing: hope for cystic fibrosis?
Free Editorial on gene editing as a potential therapeutic approach for cystic fibrosis.
The primary defect in cystic fibrosis is the result of a mutation to a single gene, CFTR, making it a prime target for gene therapy. In this free-to-access Regenerative Medicine Editorial, author Brian R Davis from University of Texas Health Science Center (TX, USA) looks at different gene-editing approaches for cystic fibrosis.
David BR. Fixing stem cells via genome editing: hope for cystic fibrosis? Regen. Med. 11(1), 1–3, doi:10.2217/rme.15.84 (2016).