Fixing stem cells via genome editing: hope for cystic fibrosis?

Written by Regenerative Medicine

Free Editorial on gene editing as a potential therapeutic approach for cystic fibrosis. The primary defect in cystic fibrosis is the result of a mutation to a single gene, CFTR, making it a prime target for gene therapy. In this free-to-access Regenerative Medicine Editorial, author Brian R Davis from University of Texas Health Science Center (TX, USA) looks at different gene-editing approaches for cystic fibrosis. David BR. Fixing stem cells via genome editing: hope for cystic fibrosis? Regen. Med. 11(1), 1—3, doi:10.2217/rme.15.84 (2016).

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